Resources SMA. Spinal Muscular Atrophy Clinical Research Center.


This website is supported by the CDC Division of Human Development and Disability Grant Number 1H75DD000473-01

Neuromuscular Diseases Resources

- Duchenne Muscular Dystrophy

- For Clinical Trials in Duchenne Muscular Dystorphy contact:
Ameneh Onativia at

- Glut1 Deficiency

- For Clinical Trials in Glut1 Deficiency contact:
Kayla Cornett at

- For Mitochondrial Diseases contact:
Jasim Uddin (clinical trial information) at
Kristen Engelstad (genetic information and additional information) at

top sma links top