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This website is supported by the CDC Division of Human Development and Disability Grant Number 1H75DD000473-01
©2007
Columbia University
Department of Neurology
SMA Clinical Research Center
updated December 8, 2017
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Neuromuscular Diseases Resources
-
Duchenne Muscular Dystrophy
- For Clinical Trials in Duchenne Muscular Dystorphy contact:
Ameneh Onativia at
am2959@cumc.columbia.edu
-
Glut1 Deficiency
- For Clinical Trials in Glut1 Deficiency contact:
Kayla Cornett at
kmc2279@cumc.columbia.edu
-
For Mitochondrial Diseases contact:
Jasim Uddin (clinical trial information) at
ju2189@cumc.columbia.edu
Kristen Engelstad (genetic information and additional information) at
ke4@cumc.columbia.edu
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