News And Staff Publications

News in SMA

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Staff Publications

• Six Minute Walk Test Demonstrates Motor Fatigue in Spinal Muscular Atrophy.
  
  
• Scoliosis surgery in children with neuromuscular disease: Finding from the US National inpatient sample.
  
  
• Reliability of telephone administration of the PedsQL Generic Quality of Life Inventory and Neuromuscular Module in Spinal Muscular Atrophy.
  
  
• Increased fat mass index in patients with spinal muscular atrophy.
  
  
• Clinical Outcome Measures in Spinal Muscular Atrophy.
  
  
• Spinal Muscular Atrophy.
  
  
• Learning to Walk: challenges for spinal muscular atrophy clinical trials.
  
  
• The changing natural history of spinal muscular atrophy type 1
  
  
• An expanded version of the Hammersmith Functional Motor Scale for SMA II and III patients
  
  
• Issues in SMA clinical trial design The International Coordinating Committee (ICC) for SMA Subcommittee on SMA Clinical Trial Design
  
  
• Challenges and opportunities in clinical trials for spinal muscular atrophy